Benefiting from technological and conceptual groundwork and positive early data, gene therapies are advancing in the clinic ...

Common measurements for modified adeno-associated viruses (AAVs), a gene therapy delivery method, showed substantial ...

A study published in Human Gene Therapy has involved the generation of a human monoclonal antibody (mAb) directed against ...

Dyno Therapeutics announces exercise of option by Roche for next-generation AAV vector for neurological gene therapy ...

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The Haslam family knew early on that their 10-year-old and 12-year-old were suffering from muscular dystrophy, but what they didn't know is that one day, the University of New Mexico Hospital would ...

The science has proven that gene therapies are effective treatments, and they have given hope to patients and their families ...

A new study published in the peer-reviewed journal Human Gene Therapy involved the generation of a human monoclonal antibody ...

Few fields in medicine are as promising and complex as gene therapy. As researchers race to develop cures for previously ...

A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...

Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA ...

Researchers have developed a highly efficient gene editing therapy that could potentially treat Stargardt disease, the most ...