"We have about eight patients that are in the insurance approval process," she said, for gene therapy treatments for beta thalassemia and sickle cell disease. "It's something that we do expect to ...
The strategic shift will allow the firm to focus on advancing a newly announced in vivo gene-editing therapy candidate that's in preclinical development.
Detroit — The Detroit Medical Center has begun treating patients with the first gene therapy for beta-thalassemia, a rare blood disorder that causes anemia and often requires regular blood ...