Cystic fibrosis (CF) is a life-threatening genetic disease affecting multiple organ systems, with pancreatic dysfunction representing a critical and often overlooked complication.

People with cystic fibrosis have better treatment options ... but the Foundation is also enthusiastic about technologies like CRISPR Cas9 to selectively correct mutated genome sequences.

New breakthroughs in gene editing mean that cures for genetic diseases such as cystic fibrosis could be developed in the near ...

CRISPR is a powerful gene-editing tool that holds enormous potential for treating genetic diseases by allowing scientists to ...

We are actively working to discover and develop cystic fibrosis mRNA therapies with Moderna Therapeutics, based in Cambridge, Massachusetts, United States, gene editing of CFTR with CRISPR ...

The programs leverage Intellia’s proprietary CRISPR-based gene editing platform ... 1b multi-dose study in people with CF. About Cystic Fibrosis Cystic fibrosis (CF) is a progressive genetic ...

The drugmaker also is exploring the use of CRISPR in several preclinical programs. It's researching in vivo therapies targeting rare genetic diseases, including cystic fibrosis and Duchenne ...

Vertex Pharmaceuticals (NASDAQ: VRTX) is a biotechnology company with a strong track record of success in developing ...

Cystic fibrosis (CF) is a life-threatening genetic disease affecting multiple organ systems, with pancreatic dysfunction representing a critical and ...

Vertex Pharmaceuticals (NASDAQ:VRTX) is a biotechnology company with a strong track record of success in developing treatments for cystic fibrosis (CF). Vertex is strategically expanding into the ...

This technology aids in the treatment of rare genetic diseases like sickle cell anemia, cystic fibrosis, and point mutation correction, as well as chronic diseases like lung cancer. Factors ...