Dystrophin and β-dystroglycan are components of the dystrophin–glycoprotein complex (DGC), a multimolecular assembly that spans the cell membrane and links the actin cytoskeleton to the ...
Duchenne muscular dystrophy (DMD) is one of the most common and devastating childhood genetic disorders, affecting ...
EDO51, an investigational therapy for Duchenne muscular dystrophy (DMD), and is still ongoing in the United Kingdom.
Children born with the degenerative disease have a genetic mutation that stops them producing dystrophin, a protein that is vital for muscle strength and function. The same disorder also occurs in ...
It may help restore muscle function and, ultimately ... been seen as a muscle problem caused by a missing protein called dystrophin," said Chang. "But new research, including our own, shows ...
A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle ...