but so unlikely as to be an unnecessary distraction from the pursuit of effective in utero and postnatal gene therapy. Data on gonadal and germ cell vector transfer is relatively easy to gather ...

Research in the field of human gene therapy is directed towards correcting genetic defects of somatic cells i.e., cells that do not contribute to the next generation. Human germ line therapy is ...

The three-year partnership is another example of Vertex’s interest in improving on Casgevy, its CRISPR medicine for sickle cell and beta thalassemia.

A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...

I recently watched an episode of one of my favourite TV shows, the Good Doctor. The episode revolved around how a man named Wyatt was rushed into the ER as he had a perforated valve and needed ...

Drexel's Master of Science in Biomedicine and Cell and Gene Therapy program offers a unique graduate-level opportunity for students at the intersection of medicine and bioengineering. An ever-evolving ...

Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA ...

Branden would be the first person in the world to receive base editing for sickle cell disease, and among the first to receive this method of gene therapy for any condition. Branden agreed to take ...

According to Dimension Market Research, the Cell and Gene Therapy Market size is expected to reach USD 22.8 billion by 2024 and is further anticipated to reach USD 111.4 billion by 2033.

In a new study, scientists combined strategies to deliver energy-disrupting gene therapy using nanoparticles manufactured to zero in only on cancer cells. Experiments showed the targeted therapy ...

most people saw gene therapy as simply a different kind of treatment for disease. However, debate continues about the ethical implications of changing germ-line cells (eggs or sperm), which would ...