Mucopolysaccharidosis type 1, also known as Hurler syndrome, is a rare but life-threatening genetic condition. Babies born with this inherited disorder do not produce an enzyme needed to break down ...

Interest in lysosomal storage diseases (LSDs) has increased significantly, because several new therapeutics received FDA approval in 2003. Though long overlooked by most major pharmaceutical ...

Oct. 23, 2024 — Long-term exposure to arsenic in water may increase cardiovascular risk and especially heart disease risk even at exposure levels below the federal ... Oct. 17, 2024 — Initial ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

Once the nymphs feed on a host, they change into adults. Hard ticks carry the germs that cause Lyme disease, Rocky Mountain spotted fever, and other diseases. Their bite doesn’t hurt.

he said. Cirrhosis can occur in the late stages of metabolic dysfunction-associated steatotic liver disease, or MASLD, which happens when fat builds up in the liver and can lead to inflammation ...

Popular Diabetes and Weight-Loss Drug May Reduce Risk of Alzheimer's Disease Oct. 24, 2024 — Researchers have found that semaglutide may lower the risk of Alzheimer's disease in people with type ...

Previously, she worked as an infectious diseases epidemiologist and global health security adviser supporting various US government agencies, multilateral organizations, and private research ...

Ten presentations at ESGCT 2024 detail the therapeutic potential and applicability of the company’s platform in rare neurometabolic diseases and ...

CLARE ATTACKER SHANE O’Donnell, Cork midfielder Darragh Fitzgibbon, and Limerick defender Kyle Hayes are the three players in the running for the 2024 Hurler of the Year award. The trio have ...

The Boston Red Sox have just two games left in the 2024 Major League Baseball regular season. Boston currently has an 80-80 record and has just two more games left in order to attempt to finish ...

The Milwaukee Brewers pitching staff may retain one of their key members of the 2024 season. Following the trade of Corbin Burnes to the Baltimore Orioles last winter, Milwaukee's pitching staff ...