Columnist Shalom Lim celebrates a new beginning in a new job, where his mission to serve fellow patients with muscular ...

Bionews, Inc., the parent company of this site, has partnered with the following nonprofit advocacy organizations to help further the mission of ensuring that patients and caregivers are able to get ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

So we have to change society. It’s a tall order, but it’s been done over and over again throughout history. It starts with a ...

Hurricanes in the southeastern U.S. prompt columnist Robin Stemple, who has FSHD, to consider his emergency preparedness plan ...

Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...

Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...

The Critical Path Institute will lead a new task force to advance the development of therapies for limb-girdle muscular ...

Columnist Betty Vertin, watching her son Chance complete his final season, wishes her sons with DMD could've played football, too.