London-based biotech Purespring Therapeutics plans to bring their kidney-tweaking gene therapy to the clinic with the help of ...

The company's primary product is H.P. Acthar Gel, an injectable drug for the treatment of proteinuria in the nephrotic syndrome of the idiopathic type, or NS, the treatment of acute exacerbations ...

Methods Patients with nephrotic syndrome (NS), antineutrophil cytoplasmic antibody-associated vasculitis ... Modulation of glucose metabolism may offer novel immune-modulatory therapeutic approaches ...

Expert opinions were elicited from rheumatologists who have expertise in the reproductive health of individuals with RMDs to build new understanding around diagnosis or treatment approaches. The cases ...

Another ultra-rare therapy will soon be subject to the gaze of an FDA advisory committee, with the fate of more than 200 boys diagnosed with Barth syndrome worldwide in the balance. On Thursday ...

The antiphospholipid syndrome (APS) is an autoimmune, multisystemic disorder associated with recurrent thrombosis (arterial and/or venous) and pregnancy loss, among other clinical manifestations.

Although more common in adults, young ones can also develop this condition through unhealthy lifestyles and genetic ...

Purespring Therapeutics raises £80/$105 million in a Series B financing to transform the treatment of kidney diseases ...

Rett syndrome (RTT) is a rare, severe, and progressive disorder that mostly affects girls of all races. It can impact your child’s ability to speak, walk, eat, or breathe easily. It was named ...