A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for ...
Studies involving the selective restoration of membrane bound nNOS to dystrophin-deficient skeletal muscle will address some of these issues. In addition to shedding light on the function of the ...
A new study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for understanding and ...
Revidia Therapeutics Inc., a cardiac regenerative medicine company developing first-in-class small molecule drug therapies for heart injury, has announced that it has expanded its leadership team in ...
Newer therapies like PGN-EDO51 that target exon skipping are considered promising pathways to slow disease progression by restoring partial dystrophin function.
This is due to a fault in the gene producing dystrophin. Muscles to become weaker ... it affects the ability to breathe as well as the function of the heart, as the heart is a muscle too.
Pfizer has reported that its Phase III CIFFREO clinical trial of investigational mini-dystrophin gene therapy ... no significant improvement in motor function was observed in the gene therapy ...