Rocket’s lentiviral (LV) vector-based hematology portfolio consists of late-stage programs for Fanconi Anemia (FA), a difficult-to-treat genetic disease that leads to bone marrow failure (BMF ...
The remaining 2 were successfully treated with 40 mg. of prednisone daily. After the hemolytic anemia was controlled the amount of steroid administered was reduced, and the patients were ...
Patients with XLSA experience a disruption in heme synthesis, leading to a spectrum of issues such as severe anemia and iron overload, which can cause symptoms like extreme fatigue, shortness of ...
Eltrombopag olamine is under development for acute myelocytic leukemia, chronic immune (idiopathic) thrombocytopenia (ITP), Fanconi anemia, severe aplastic anemia and hematopoietic sub-syndrome of ...
This kind of cut is the most common reason for emergency room visits in the United States. Several million cases are reported each year. While a laceration can often be deep, you may be able to treat ...