The science has proven that gene therapies are effective treatments, and they have given hope to patients and their families ...

Joe DePinto, MBA, discussed the findings of the McKesson 2024 Cell and Gene Therapy Report, providing insight into the ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

What's on the horizon for the life sciences industry? Robin Johnson, PharmD, Gene Therapy Submissions Lead, inSeption Group What unique challenges do gene therapy submissions face compared to ...

Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...

Researchers at the Experimental and Clinical Research Center in Berlin are developing a targeted treatment for muscular ...

Nanoscope Therapeutics is on the brink of filing for FDA approval of what could be the first gene therapy for incurable eye disease retinitis pigmentosa (RP) that can be used regardless of ...

Blood centres cannot make cell therapies more accessible on their own. For decades they have partnered with hospitals to ...

Researchers at the Experimental and Clinical Research Center (ECRC), a joint institution of the Max Delbrück Center and Charité—Universitätsmedizin Berlin, have developed a promising gene-editing ...

Microbial neutralization must constantly achieve a six-log reduction threshold of Geobacillus stearothermophilus and comply ...

But it takes more than one step to get from gene to protein, and the process of building proteins is a key step in the gene expression ... Specific patterns of gene expression may define tumor ...

Capable of precisely editing genes, activating gene expression and repressing genes all at the same time, the ...