A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...

β-Thalassemia is a genetic disorder characterized ... Diagnosing iron overload involves several parameters, with serum ...

Eligibility for the TLC study included patients with all thalassemia syndromes who required ... depression), self-reported adherence, and average ferritin and LIC in the past year (both log ...