New medications and gene therapy are helping to prolong life in other types of SMA, but they tend to work best when disease symptoms are not already severe, as they are in infants with SMA type 0.
or Werdnig-Hoffmann disease. Syndrome-associated scoliosis is observed in Neurofibromatosis, Marfan's syndrome, and thoracic wall deformities or postcardiac/thoracic wall surgery.
June 10, 2024 — Scientists have grown 'mini-guts' in the lab to help understand Crohn's disease, showing that 'switches' that modify DNA in gut cells play an ... Major Cause of Inflammatory ...
Jan. 2, 2025 — Patients diagnosed with late-stage or metastatic breast cancer have a statistically significant increased risk of pre-diagnosis cardiovascular disease (CVD) compared to those with ...
Labor can increase the risk for compromised oxygenation in the fetus. Uterine contractions produce transient decreases in blood flow to the placenta, which can lead to interruptions in gas ...
RG-6631 is under clinical development by F. Hoffmann-La Roche and currently in Phase II for Crohn’s Disease (Regional Enteritis). According to GlobalData, Phase II drugs for Crohn’s Disease (Regional ...
This unsettling event has reignited discussions about “Disease X.” Disease X is not an actual but a hypothetical disease. The World Health Organization (WHO) coined the term in 2018 to ...
Zinpentraxin alfa is under clinical development by F. Hoffmann-La Roche and currently in Phase I for Crohn’s Disease (Regional Enteritis). According to GlobalData, Phase I drugs for Crohn’s Disease ...
A previously unknown disease making the rounds in the Democratic Republic of Congo (DRC) is a severe form of malaria, the country’s health ministry has announced. Health authorities on Tuesday ...