Duchenne muscular dystrophy (DMD) is one of the most common and devastating childhood genetic disorders, affecting ...

EDO51, an investigational therapy for Duchenne muscular dystrophy (DMD), and is still ongoing in the United Kingdom.

Percheron Therapuetic's key trial for Duchenne muscular dystrophy has flopped, sending the shares into freefall ...

Sevasemten significantly reduced two markers of muscle damage in treated Becker muscular dystrophy patients in Phase 2 CANYON ...

Delandistrogene moxeparvovec uses an adeno-associated viral (AAV) vector to deliver a micro-dystrophin transgene ... Long-Term Survival and Myocardial Function Following Systemic Delivery of ...

Click here to read the article now. Delandistrogene moxeparvovec uses an adeno-associated viral (AAV) vector to deliver a micro-dystrophin transgene to skeletal and cardiac muscle. Rachel Potter ...

During the second trimester, the baby’s heart showed irregular beating, but improved as the pregnancy continued. The mother’s heart function remained stable and the baby’s heart function returned to ...

The primary endpoint of the study is the change from baseline in a 17-item test that measures motor function in boys with ... correct version of the misfolded dystrophin protein that is the ...

Dystrophin and β-dystroglycan are components of the dystrophin–glycoprotein complex (DGC), a multimolecular assembly that spans the cell membrane and links the actin cytoskeleton to the ...