Locals in Clonmel, Co Tipperary, been left heartbroken by the death of Little Blue Hero and Honorary Garda Tadhg Relihan.
Hari Jones from Caernarfon in Gwynedd has myotubular myopathy, which means the muscles he uses to breathe and swallow do not work. Merseyside Police gave him a guard of honour as he left on Tuesday.
In a study of gene therapy for X-linked myotubular myopathy, patients required high doses of the adeno-associated viral (AAV) vector to ensure that enough genetic material could reach the skeletal ...
The write-down comes in the wake of problems affecting the Japanese drugmaker's AT132 gene therapy candidate for rare disease X-linked myotubular myopathy (XLMTM), which was placed on clinical ...
The community of Clonmel is heartbroken following the death of little Tadhg Relihan, an Honorary Garda. Tadgh and his twin ...
There has been a fourth patient fatality in Astellas' clinical trial of its AT132 gene therapy for the rare disease X-linked myotubular myopathy (XLMTM), which has been halted twice due to safety ...
This is one of thousands of bunting flags that were made into the world's longest line (now in the world records) to raise money for myotubular myopathy, which my best friend's brother has.